Amicus Therapeutics | Advancing Therapies to Treat Rare Diseases
A Rare Story

We Believe In Our Future.

Read more about Pompe Disease

Noah, 10 Living with Pompe Disease Read story
A Rare Journey

Our Families are Part of the Amicus Experience.

Megan, 24 Living with Pompe Disease
A Rare Community

Amicus Global Research and Gene Therapy Center of Excellence in Philadelphia.

New state of the art research facility builds on the city's 250-year tradition of medical innovation.

Read more

A Rare Commitment

To Ensuring Patient Access to Medicines.

Read more about our Expanded Access Program

Michael, 25 Living with Fabry Disease

About Amicus

We are a biotechnology company at the forefront of advanced therapies to treat a range of devastating rare diseases.

News & Announcements

CEO & Chairman John F. Crowley Delivers Notre Dame Commencement Address.

Programs & Pipeline

Programs & Pipeline

We are leveraging our innovative technology platforms to develop treatments for human genetic diseases.

More
Rare Stories

Rare Stories

Be inspired by people living with rare disease across the globe.

More
Career @ Amicus

Career @ Amicus

Join a team committed to changing the lives of patients with rare metabolic diseases. Now hiring in multiple locations.

More