Amicus Therapeutics | Advancing Therapies to Treat Rare Diseases

Our passion for making a difference unites us.

Amicus Therapeutics is a global, patient-dedicated biotech focused on discovering, developing, and delivering high-quality medicines for people living with rare metabolic



KatelynnAge 11

Living with CDKL5 Deficiency Disorder

Read her story ›

About Amicus

We are a biotechnology company at the forefront of advanced therapies to treat a range of devasting rare diseases.

Extraordinary Patient Focus

Extraordinary Patient Focus

At Amicus, patient-centricity is in our DNA. See how our commitment to patients goes further than just our medicines and expands out to the rare disease community at large.