Katelynn, Age 10
Living with CDKL5 Deficiency Disorder (CDD)
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For more information on Batten disease, please refer to the following resources:
Information for patients and families about participating in clinical trials is available at the following websites:
The following websites offer additional information and support for individuals and families living with Batten disease:
Information for patients and families about participating in clinical trials is available at the following websites:
The following websites offer additional information and support for individuals and families living with CDD:
Important Information for Patients About SD-101 for Epidermolysis Bullosa
For more information on EB, please refer to the following resources.
Information for patients and families about participating in clinical trials is available at the following websites:
The following websites offer additional information and support for individuals and families living with EB:
For information on Fabry disease, please refer to the following resources:
Information for patients and families about participating in clinical trials is available at the following websites:
The following websites offer additional information and support for individuals and families living with Fabry disease:
For additional information on Pompe disease, please refer to the following resources:
Information for patients and families about participating in clinical trials is available at the following websites:
The following websites offer additional information and support for individuals and families living with Pompe disease:
Be inspired by people living with rare disease across the globe.